A Medical First: Baby Cured by Gene-Editing Therapy Led by Indian-Origin Scientist Dr. Kiran Musunuru
A Historic Breakthrough: World’s First Gene-Editing Cure Saves Infant’s Life In a landmark advancement in modern medicine, a nine-month-old baby diagnosed with a rare and life-threatening genetic disorder has been cured using the world’s first customised gene-editing therapy. The baby, identified as KJ, was suffering from severe CPS1 deficiency — a rare metabolic condition affecting…



